Sharon J Brown
Gene therapy for spinal muscular atrophy: perspectives on the possibility of optimizing SMN1 delivery to correct all neurological and systemic perturbations
Brown, Sharon J; Yáñez-Muñoz, Rafael J; Fuller, Heidi R
Citation
Brown, S. J., Yáñez-Muñoz, R. J., & Fuller, H. R. (2024). Gene therapy for spinal muscular atrophy: perspectives on the possibility of optimizing SMN1 delivery to correct all neurological and systemic perturbations. Neural Regeneration Research, https://doi.org/10.4103/NRR.NRR-D-24-00504
| Journal Article Type | Article |
|---|---|
| Acceptance Date | Jun 14, 2024 |
| Online Publication Date | Jul 29, 2024 |
| Publication Date | Jul 29, 2024 |
| Deposit Date | Jun 25, 2024 |
| Publicly Available Date | Jun 26, 2024 |
| Journal | Neural Regeneration Research |
| Print ISSN | 1673-5374 |
| Electronic ISSN | 1876-7958 |
| Publisher | Medknow Publications |
| Peer Reviewed | Peer Reviewed |
| DOI | https://doi.org/10.4103/NRR.NRR-D-24-00504 |
| Public URL | https://keele-repository.worktribe.com/output/857679 |
Files
Gene Therapy For Spinal Muscular Atrophy: Perspectives On The Possibility Of Optimizing SMN1 Delivery To Correct All Neurological And Systemic Perturbations
(2.2 Mb)
PDF
Licence
https://creativecommons.org/licenses/by-sa/4.0/
Publisher Licence URL
https://creativecommons.org/licenses/by-sa/4.0/
Copyright Statement
The final version of this accepted manuscript and all relevant information related to it, including copyrights, can be found on the publisher website.
You might also like
Pathogenic variants in LINC complex-associated genes
(2024)
Journal Article
State of the Art in Sub-Phenotyping Midbrain Dopamine Neurons
(2024)
Journal Article
Proteomic characterization of human LMNA-related congenital muscular dystrophy muscle cells
(2024)
Journal Article
Downloadable Citations
About Keele Repository
Administrator e-mail: research.openaccess@keele.ac.uk
This application uses the following open-source libraries:
SheetJS Community Edition
Apache License Version 2.0 (http://www.apache.org/licenses/)
PDF.js
Apache License Version 2.0 (http://www.apache.org/licenses/)
Font Awesome
SIL OFL 1.1 (http://scripts.sil.org/OFL)
MIT License (http://opensource.org/licenses/mit-license.html)
CC BY 3.0 ( http://creativecommons.org/licenses/by/3.0/)
Powered by Worktribe © 2024
Advanced Search